Inspired by patients and families living with a rare disease
Being diagnosed with a rare disease can feel overwhelming and isolating. We understand the power of connecting with the right care team and with others facing similar circumstances. That’s why we strive to foster that feeling of community—connection and contribution—within our clinical studies.
We believe each unique challenge and complexity represents an opportunity to show our agility and value. Together, with the engagement and inclusion of patients, families, and the broader community, we’re committed to helping advance new orphan drugs for rare diseases.